MedPage Today1d
Lentiviral Gene Therapy Shows Promise in Severe Hemophilia A
SAN DIEGO -- Results from a small single-center study showed that treatment with a gene therapy involving the use of ...
eLife22h
Rab10 inactivation promotes AMPAR insertion and spine enlargement during long-term potentiation
Among these sensors, we further focused on the spatiotemporal dynamics of Rab10 and Rab4 activity during sLTP. We found that postsynaptic stimulation leads to the persistent inactivation of Rab10 and ...
Hemogenyx Pharmaceuticals PLC Announces CBR Macrophage Delivery Update
Breakthrough in Delivering Chimeric Bait Receptors to Immune Cells Accelerates Development LONDON, UK / ACCESSWIRE / December ...
EsoBiotec Begins Clinical Trial of In Vivo BCMA CAR-T Candidate ESO-T01 for Multiple Myeloma
ESO-T01 is the first in vivo BCMA CAR-T candidate to reach the clinical stageEarly clinical data are expected in second half of ...
BMJ5d
Practical approach to the diagnosis of adult-onset leukodystrophies: an updated guide in the genomic era
Recently, gene correction has also shown promise. In principle, gene correction (eg, through lentiviral transduction of the patient’s own cells) should be possible in most loss of function genetic ...