This causes symptoms that are moderate to severe. Alpha thalassemia major (hydrops fetalis with Hemoglobin Barts), which is a rare condition in which all four genes are missing or mutated.

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And globally, we now think that there is 30,000 odd severe patients in the Middle East, both sickle cell and thalassemia. And we're even finding out that there are a lot more sickle cell patients ...

Sometimes, people with iron deficiency anemia don't respond to treatment with iron supplementation and may go months to years with little to no improvement in anemia. This can happen if the dose is ...

Beam Therapeutics (NASDAQ:BEAM – Get Free Report)‘s stock had its “buy” rating reiterated by stock analysts at HC Wainwright ...

It develops BEAM-101 for the treatment of sickle cell disease or beta-thalassemia; and BEAM-302, a liver-targeting LNP ...