gene therapy, Haemophilia A

Indian scientists develop 1st human gene therapy for Haemophilia A
In a significant medical feat, Indian scientists have developed the first-in-human gene therapy using lentiviral vectors for severe haemophilia A
DBT, CSCR develop 1st human gene therapy for Haemophilia A in India
Haemophilia is a severe bleeding disorder caused by the deficiency of clotting Factor VIII, leading to spontaneous internal and external bleeding episodes
Gene therapy brings new hope for haemophilia patients
BHUBANESWAR: In a significant medical breakthrough, India's first human gene therapy with a lentiviral vector for severe haemophilia-A has been found to be successful with zero bleeding rate in patients.
DBT & CSCR executes India’s first Human Gene Therapy for Hemophilia A patients
In the groundbreaking study the researchers observed an annualised zero bleeding rate in all the five subjects enrolled with the production of Factor VIII for a prolonged period of time thus obviating the need for repeated infusions.
India makes big breakthrough in treating genetic disorder Hemophilia A
India has successfully conducted its first in-human gene therapy for hemophilia A, with patients experiencing no bleeding episodes post-treatment.
Indian scientists develop novel gene therapy treatment for haemophilia
Indian scientists successfully use gene therapy to treat severe haemophilia A, a rare hereditary condition with promising results.
MedPage Today1d
Lentiviral Gene Therapy Shows Promise in Severe Hemophilia A
SAN DIEGO -- Results from a small single-center study showed that treatment with a gene therapy involving the use of ...
The Financial Express11h
First-in-human indigenous gene therapy for Hemophilia A shows significant positive outcomes
Current treatments require frequent Factor VIII replacement therapy, which faces challenges such as high costs, venous access ...
Medscape8d
Retroviral Vectors for Gene Therapy
Lentiviral self-inactivating vectors are the retroviral vectors with the greatest potential for gene therapy Nondividing cells can be transduced by lentiviral vectors. They possess a low ...
EurekAlert!22d
A new strategy to enhance gene therapy for sickle cell disease
Researchers described a promising new approach for using gene therapy to treat sickle cell disease in the peer-reviewed journal Human Gene Therapy. To improve the efficacy of gene therapy ...
FiercePharma9d
FDA considers 'regulatory action' for bluebird's Skysona after blood cancer reports
The FDA notification came seven weeks after the New England Journal of Medicine (NEJM) published a report that seven of 67 ...
Morningstar7d
VIVEbiotech Secures Growth Investment from Ampersand Capital Partners to Expand Lentiviral Vector Development and Manufacturing Capabilities
manufacturing and analytical testing for leading biopharmaceutical companies engaged in gene therapy and cell therapy projects. With a specific focus on lentiviral vector production, the ...