Prenatal gene therapy via mRNA LNPs fixes faulty genes in fetal brain cells in animal model of neurodevelopmental syndrome.

A single treatment with, a CRISPR-Cas9 based gene editing therapy, is enough to replace the daily medication of patients with ...

Some prior research had shown that gene therapy would not lower the amount of time children spend on ventilator support.

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Acquisition creates a leading, clinical-stage company focused on the development of gene therapy treatments for rare inherited retinal degenerations New OPGx-LCA5 Phase 1/2 6-month data demonstrate sa ...

Positive results for Intellia Therapeutics, Inc.'s NTLA-2002 in treating HAE patients. Stock price dips, but the program ...

Lyell Immunopharma has entered a definitive agreement to acquire ImmPACT Bio, a privately-owned clinical-stage biotechnology ...

Intellia has reported positive results from its ongoing Phase I/II trial of NTLA-2002, a CRISPR-based gene editing therapy ...

Dyno Therapeutics has formed a new research partnership with Roche, focusing on the development of next-generation ...

CHILDREN in Spain who have been deaf from birth are hearing for the first time after taking part in gene therapy trials. Four ...

Medera Inc. today announced that its clinical-stage gene therapy subsidiary, Sardocor Corp., has successfully completed its ...

So, we’re voting, and the outcome may end the world, or not. So, we’re voting, and just reading the news this morning put me ...