Data in a newly released study on Sarepta Therapeutics Duchenne therapy diverge from the company line, @adamfeuerstein writes ...

A Pfizer result is unsettling the gene therapy push for Duchenne muscular dystrophy: The boys didn't improve even though a ...

Standard zinc supplementation had limited impact on muscle health or zinc levels in boys with Duchenne muscular dystrophy, ...

New Gene Therapy Approach Shows Promise for Duchenne Muscular Dystrophy July 24, 2024 — Researchers have made a significant breakthrough in developing a new gene therapy approach that restores ...

The film focuses on a Norwegian gamer who died at 25, leaving behind a richer online life than his family could have imagined ...

A Phase 3 clinical trial investigating Elevidys (delandistrogene moxeparvovec), a gene therapy for Duchenne muscular ...

Support CureDuchenne with WoW’s Revenant Pack! Get exclusive mounts and a pet while contributing to a great cause.

On Saturday 21 September, Nathan Franklin, 31, and his friend Tom Grassby, 31, from Leeds, ran 53 miles – the equivalent of ...

Inspired by "The Remarkable Life of Ibelin" Documentary, Players in World of Warcraft can Support Global Nonprofit and Fund ...

Joseph Schwartz, an analyst from Leerink Partners, maintained the Buy rating on Solid Biosciences (SLDB – Research Report). The ...

Tearjerkers don’t come much more effective than The Remarkable Life of Ibelin, a story about a young boy’s death and, also, ...

The Killian family, of Rockwall, are celebrating a record-breaking fundraising milestone with their annual Sam's Night event, ...