Roche Holding AG is willing to pay more than $1 billion to solve one of the biggest challenges of gene therapy: delivery.The ...
STAT's Readout LOUD podcast discusses Pfizer's woes, explains RFK Jr.'s 'MAHA' campaign, and mulls the latest about the Novo ...
The incubator is designed to draw cell and gene therapy researchers and drugmakers to work at the hub, where they can develop ...
Prenatal gene therapy via mRNA LNPs fixes faulty genes in fetal brain cells in animal model of neurodevelopmental syndrome.
After 44 days, Kendric Cromer, 12, left the hospital. While his family feels fortunate that he was the first to receive a ...
Medpage Today on MSN2d
Gene-Editing Therapy Reduced Attacks in Hereditary AngioedemaA single dose of the CRISPR-based gene-editing therapy NTLA-2002 reduced angioedema attacks and led to sustained reduction in ...
Sep. 25, 2024 — Adults with hemophilia B saw their number of bleeding episodes drop by an average of 71 percent after a single infusion of gene therapy, according to the new results of an ...
Some prior research had shown that gene therapy would not lower the amount of time children spend on ventilator support.
News Medical on MSN12h
Single treatment with CRISPR gene editing therapy offers hope for hereditary angioedema patientsA single treatment with, a CRISPR-Cas9 based gene editing therapy, is enough to replace the daily medication of patients with ...
Data in a newly released study on Sarepta Therapeutics Duchenne therapy diverge from the company line, @adamfeuerstein writes ...
Eye drug maker Ocuphire Pharma is acquiring gene therapy developer Opus Genetics in an all-stock transaction that will see ...
Medpage Today on MSN3d
Evidence of Durable Vision Improvement With Gene Therapy for Retinitis PigmentosaCHICAGO -- A mutation-agnostic gene therapy for retinitis pigmentosa (RP) showed promise for improving vision in severely ...
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